Source: GlobeNewswire

Press Release: LogicBio : LogicBio Therapeutics Receives Rare Pediatric Disease Designation for LB-001 for the Treatment of Methylmalonic Acidemia

CAMBRIDGE, Mass., July 16, 2019 (GLOBE NEWSWIRE) -- LogicBio Therapeutics, Inc. (NASDAQ:LOGC), a genome editing company focused on developing medicines to durably treat rare diseases in pediatric patients, today announced the U.S. Food and Drug Administration (FDA) has granted rare pediatric disease designation to LB-001, a recombinant adeno-associated viral vector with human methylmalonyl-COA mutase (MUT) gene for the treatment of methylmalonic acidemia (MMA). In addition to rare pediatric disease designation, LogicBio previously received orphan drug designation from the FDA for LB-001.

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Frederic Chereau's photo - President & CEO of LogicBio

President & CEO

Frederic Chereau

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82/100

LogicBio is a biotechnology company that develops genetic medicines to treat rare pediatric diseases. Read more